Ep. 291: “Functional Precision Medicine” Featuring Dr. Scott Younger

Dr. Scott Younger, Director of Disease Gene Engineering at Children’s Mercy Hospital, dives into the world of functional precision medicine. He reveals how personalized antisense oligonucleotides can reverse disease phenotypes in organoid models of Duchenne muscular dystrophy. Younger emphasizes the importance of his lab's connections to the rare disease community, fostering collaboration with clinicians. The discussion highlights innovative approaches to personalized therapies, addressing the challenges of accessibility and costs in advanced healthcare.