Ep. 137: New Horizons on Treatment Choices of Rare Disorders

Moderator: Justyna Paprocka (Katowice, Poland)

Guests: Laurent Servais (Oxford, UK), Michelangelo Mancuso (Pisa, Italy)

In this first March episode, Paprocka, Mancuso, and Servais explore groundbreaking advancements in treating rare neurological disorders, focusing on paediatric and adolescent neurology. They discuss the role of gene therapy, emerging treatment strategies for neuromuscular disorders, and the evolving challenges of transitioning care from paediatric to adult neurology.