The chapter explores the significance of rare diseases in gene therapy and the passion and mission-driven focus required to tackle them. It discusses the financial incentives and timeline for startups in the field, highlighting the importance of long-term goals rather than immediate profitability. The chapter also delves into specific genetic diseases, their variations, and the potential for gene therapy to address childhood diseases and prevent chronic lifestyle diseases.
Are rare diseases themselves rare? Neil deGrasse Tyson and comedian Chuck Nice learn about the science of gene therapy and how it can treat and potentially cure rare diseases with Gaurav Shah, CEO, Rocket Pharma.
NOTE: StarTalk+ Patrons can listen to this entire episode commercial-free here:
https://startalkmedia.com/show/unlocking-gene-therapy-with-gaurav-shah/
Thanks to our Patrons Ernesto Rodriguez, James Lewandowski, Juan Cornejo, Shane, Hayden Christensen, jacob vine, and Calina Lungu for supporting us this week.
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