Mila Makovec
The first person in the world to be treated with a medicine created just for her.
Best podcasts with Mila Makovec
Ranked by the Snipd community
Apr 16, 2024 • 29min
Mila’s Legacy
Mila Makovec, the first person in the world treated with a medicine tailored for her, battled Batten disease with a unique drug called milasen. Her mother's relentless efforts led to fundraising millions for the treatment. Despite initial success, Mila sadly passed away at age ten, highlighting the challenges of personalized medicine for rare diseases. The podcast dives into the future of genomic medicine, discussing innovative projects in the UK and the potential for accessible genetic treatments worldwide.
