Anne Lennox

Join Anne Lennox, Founder of the Myotubular Trust, Meriel McEntagart of Genomics England, and Carlo Rinaldi from the University of Oxford as they dive into the evolving landscape of rare condition therapies. They discuss how patient communities are revolutionizing research and pushing for faster diagnoses. Hear about the transformative power of shared experiences in gene therapy and the importance of collaborative initiatives like UPNAT for equitable access. Discover the challenges and breakthroughs driving innovative treatments for rare diseases!