

Post-ASH non-malignant highlights: updates in sickle cell disease, thalassemia, and hemophilia
Feb 14, 2025
Dr. Rabi Hanna from Cleveland Clinic shares insights on innovative treatments for severe sickle cell disease. He presents updated results from the RUBY trial, highlighting the potential of reni-cel as a groundbreaking gene therapy. The conversation also touches on the promising outcomes of the HIBISCUS trial for Etavopivat, showing significant improvements in patient quality of life. Furthermore, advancements in thalassemia treatments are discussed, focusing on reduced transfusion needs from the ENERGIZE-T study.
Chapters
Transcript
Episode notes
1 2 3 4 5
Intro
00:00 • 3min
Updates on Clinical Trials for Sickle Cell Disease
02:58 • 3min
Advancements in Treating Sickle Cell Disease and Thalassemia
05:47 • 4min
Positive Outcomes from the Energize-T Study on Metapivat in Thalassemia
09:40 • 4min
Significant Reductions in Bleeding Rates with Kincisumab Prophylaxis
13:46 • 5min