A Non-Profit Biotech Model; Therapies for Rare Diseases - Dr. Ashley Winslow
Sep 9, 2023
auto_awesome
Dr. Ashley Winslow, CEO/CSO of Odylia Therapeutics, discusses a novel non-profit model for addressing rare diseases and the approaches being designed for two rare genetic eye diseases. Topics include the challenges of developing therapies for rare diseases, the founding of a nonprofit biotech company for rare disease research, gene therapy solutions for eye disorders, and the potential of gene therapy for treating Usher syndrome.
Nonprofit biotechs prioritize patient care over profits, providing innovative solutions for rare diseases.
Gene therapies using AV technology show promise for treating vision-related disorders like Leber Congenital Amaurosis (LCA) and Usher syndrome.
Deep dives
The Challenge of Rare Diseases
Rare diseases pose challenges in recruiting study participants and generating profits for big companies due to small patient populations. Small companies can provide innovative solutions for rare diseases.
Exploring the Nonprofit Model in Biotechnology
Adelia Therapeutics, a nonprofit biotech company, aims to prioritize patient care over shareholder returns. Nonprofit biotechs focus on safety, efficacy, and available technology without the need for market analysis.
Leveraging Gene Therapy for Vision Loss
Adelia Therapeutics is developing gene therapies for rare diseases like Leber Congenital Amaurosis (LCA) and Usher syndrome. Gene therapies deliver functional copies of genes to targeted cells. AV technology allows targeted delivery to the eye, making it advantageous for vision-related disorders.
The Future of Adelia Therapeutics
Adelia Therapeutics plans to expand beyond vision loss and explore other rare diseases. The company aims to be a backbone, supporting patient groups in navigating drug discovery and regulation.
This episode has two parts. The first part discusses how Odylia Therapeutics is addressing rare disease, using a novel non-profit model. The second half address two rare genetic eye diseases and the approaches being designed to address them. Dr. Ashley Winslow, CEO/CSO of Odylia, describes how a non-profit is well suited to address these rare diseases, using strategies that leverage capacities in rare disease patient communities coupled to their expertise in drug discovery.
Get the Snipd podcast app
Unlock the knowledge in podcasts with the podcast player of the future.
AI-powered podcast player
Listen to all your favourite podcasts with AI-powered features
Discover highlights
Listen to the best highlights from the podcasts you love and dive into the full episode
Save any moment
Hear something you like? Tap your headphones to save it with AI-generated key takeaways
Share & Export
Send highlights to Twitter, WhatsApp or export them to Notion, Readwise & more
AI-powered podcast player
Listen to all your favourite podcasts with AI-powered features
Discover highlights
Listen to the best highlights from the podcasts you love and dive into the full episode