
Combating misinformation in a crisis: Lessons from Deepwater Horizon
Tiny Matters
00:00
The First Gene Therapy for Children With Duchenne Muscular Dystrophy
The first gene therapy for children with Duchenne muscular dystrophy has been approved by the US FDA. This is a pretty rare disease that affects about six out of every hundred thousand people in Europe and North America. What scientists are doing is they actually have created a shortened form of the dystrophin gene. They're packing it into a harmless virus and then delivering it to muscle cells so that their shock absorption can happen normally.
Transcript
Play full episode