
Therapeutic Human Gene Editing with Dr. David Liu
FYI - For Your Innovation
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Is There a Need for Sickle Cell Disease Treatments?
300 thousand new born ayear, are born with sickle cell disease. That's more than many genetic diseases entire known human population of s. The current generation of sickle cell genetity an therites being trialled rely on ex vivo editing followed by a bone pro transplant. What's urgently needed in that target area is a way to do in vitro jan editing to permanently correct the siccle cell mutation without having to require bone marroation.
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