Intro

In a world first, a baby has been treated with a personalised gene-editing technique.

KJ’s parents were given the choice of a liver transplant or a CRISPR therapy that nobody had ever received. The journey isn’t over, but KJ has improved.

So what’s on the horizon for CRISPR therapies – will we continue to see personalised applications?

Guest/s

• Professor Marco Herold, CEO of the Olivia Newton-John Cancer Research Institute and head of the Blood Cancer and Immunotherapy Laboratory

References

• World's First Patient Treated with Personalized CRISPR Gene Editing Therapy at Children’s Hospital of Philadelphia
• Patient-Specific In Vivo Gene Editing to Treat a Rare Genetic Disease - NEJM