The Evolution of Gene Therapies: Balancing Promise and Caution

This chapter explores the advancements in gene therapies for hemophilia A and B, emphasizing the gap between scientific success and patient adoption. It discusses concerns regarding the long-term efficacy and irreversibility of first-generation gene therapies, drawing parallels to technological advancements. Additionally, the chapter delves into the challenges and benefits of CAR-T treatments for cancer, emphasizing the need for balancing risks and accessibility in personalized therapies.