358: FDA's gene therapy turmoil, and an alternative model for funding research
The Readout Loud
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Concerns Over Gene Therapy Safety and FDA Approval Processes
This chapter examines the recent patient fatalities linked to gene therapy, particularly the case of a young boy with severe liver toxicity. It delves into the FDA's decision to expedite approval for a controversial gene therapy and the ensuing safety concerns amid Sarepta's responsive actions.
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