
The treatment landscape and challenges in rare diseases: BPDCN, CMML, MPN-AP/BP, and VEXAS
VJHemOnc Podcast
00:00
Intro
This chapter explores the intricate challenges and therapeutic strategies in treating rare diseases such as BPDCN, CMML, and VEXAS syndrome. It highlights the limitations of novel therapies and discusses promising treatments like IDH and LSD1 inhibitors, emphasizing the need for effective disease control prior to potential stem cell transplants.
Transcript
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