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Revolutionizing ALS Treatment: The Tofersen Breakthrough

Neurology® Podcast

CHAPTER

Remarkable Transformation: A Patient's Journey with Tofersen

This chapter shares the inspiring story of a patient with an SAD1 mutation in a Tofersen clinical study. It details the patient's initial decline followed by a significant recovery in strength and function after switching to an open-label extension, highlighting the transformative potential of Tofersen for ALS treatment.

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