
Using Gene Therapy to Help the Blind See
What's Your Problem?
Advancements in Gene Therapy
This chapter explores the evolution of gene therapy, particularly in addressing the rare genetic condition LCA1, which causes severe visual impairment. It discusses innovative research methods using chickens as a model to test gene therapy techniques and the challenges of embryo survival. The chapter also highlights the crucial role of viral vectors, particularly adeno-associated virus (AAV), in the development of effective gene therapy solutions.
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