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Sickle Cell Disease
The cost is going to come down because it will become easier and less expensive to make the molecules that are needed for these therapeds. When we think about sickle cell disease, a big factor there is going to be delivery. How do you get the crisper cules where they're needed? The way that this treatment is done right now is using a bone marrow transplant to replace the edited cells back into the patient. But we're imagining a day when you have a delivery strategy that allows you to give a patient a one time injection or maybe some day even they just have to take a pill.