Dr. Dietrich Stephan: New Drugs that Repair Broken Genes
Talking Biotech with Dr. Kevin Folta
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Mutina Mutinitis - Is This a Prophylactic?
The drug that your company as designed identifies the codons that in code this poly nuclea tide repeat and are able to shut down transcription from those abarrent gens. And know, given an individual is born with the mutation, but doesn't develop symptoms until mid lifeit' It's a relatively slow progressing disease in the context of a life span. So if we can get an affected, often individual from an affected patient, tested early in life, cause theire family history and get in a decade before first symptom onset, we firmly believe we can push out the onset of the disease significantly by decades.
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