Trials and Triumphs: A Mother's Journey with Gene Therapy

This chapter recounts a mother's experience with her child's gene therapy treatment using Elevitus, detailing both the initial optimism and subsequent medical complications they faced. It highlights the balancing act between hope and risk, particularly in the wake of serious side effects and regulatory challenges surrounding gene therapies. The narrative culminates in a reflection on the emotional toll of navigating treatment options for Duchenne muscular dystrophy and the enduring hope for affected families.